Gene targeting techniques are used by scientists to simulate human genetic disorders in model organisms. Many scientists believe that gene targeting will lead the way to new methods for correcting genetic defects.
Pioneered by Mario Capecchi, gene targeting is a process in which scientists use embryonic stem (ES) cells to simulate genetic disorders in mice, study their development, and test new therapies. Many believe that gene targeting will lead the way to new methods for directly correcting genetic defects.
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