2D Animation of Intrathecal Drug Delivery for SMA
A 2D animation shows how drugs for SMA may be delivered to the central nervous system via intrathecal infusion into the spinal cord.
Spinal muscular atrophy, SMA, RNA, mRNA, splicing, gene, genetic, DNA, antisense, motor neuron, splice, Therapy, Intrathecal, delivery, drug, mechanism, central nervous system, spinal cord, epidural, inject, needle, cerebrospinal fluid, blood-brain barrier, vertebra, axon, dendrite
- ID: 16952
- Source: DNALC.SMA
Related Content
16951. Drug Delivery Mechanisms for SMA
Dr. Sumner explains how drugs can be delivered into the central nervous system.
16950. 2D Animation of Antisense Oligonucleotide Therapy for SMA
An animation shows how antisense oligonucleotide therapy for SMA utilizes RNA splicing.
16954. Clinical Trials for New SMA Therapies
Dr. Sumner discusses the clinical trial process for SMA antisense oligonucleotide therapy.
16941. 2D Animation of Alternative RNA Splicing
An animation shows alternate splicing of the SMN2 gene.
16931. 2D Animation of Genes and Inheritance
An animation introduces DNA and the pattern of inheritance for SMA.
16939. RNA Splicing
A step-by-step 2D animation shows the details of RNA splicing.
16909. Introduction to SMA
Dr. De Vivo provides an overview of SMA, and describes the four SMA types.
16911. A simple description of the cause of SMA
Frank, an SMA parent, describes the genetics of SMA.
16948. Alternative RNA Splicing Therapy for Spinal Muscular Atrophy
Drs. Sharp and Sumner describe how RNA splicing can be used as a therapy for SMA.
16947. Small Molecule Therapy for SMA
Dr. Sumner describes small molecule therapies for SMA.